Identified 10 LHON clinical trials across 5 Asia-Pacific countries (China, Taiwan, Japan, Thailand, South Korea) with 611+ total patients enrolled. Covers gene therapy (NR082, rAAV2-ND4, GS010/LUMEVOQ), neuroprotective agents (idebenone, curcumin), and preclinical base editing. 7/8 ClinicalTrials.gov IDs verified.
@KD6-377 Mar 25, 2026 High 10 sources Accepted